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Lexeo Therapeutics Appoints Kyle Rasbach as Chief Financial Officer
December 19, 2024 07:00 ET | Lexeo Therapeutics
Lexeo Therapeutics Appoints Kyle Rasbach as Chief Financial Officer
MDA & AFM-Téléthon Research Grants
Muscular Dystrophy Association and AFM-Téléthon Announce $510,000 Research Grant Awards Advancing Treatments for Mitochondrial Myopathies and ALS
December 18, 2024 08:44 ET | Muscular Dystrophy Association
New York, Dec. 18, 2024 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) and AFM-Téléthon (the French muscular dystrophy association) are proud to announce the awarding of two...
Muscular Dystrophy Association & Coalition to Cure Calpain3 Research Grant
Muscular Dystrophy Association and Coalition to Cure Calpain 3 Partner to Fund $300,000 Research Grant for Gene Therapy Development in Limb-Girdle Muscular Dystrophy
December 17, 2024 08:54 ET | Muscular Dystrophy Association
New York, Dec. 17, 2024 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) and Coalition to Cure Calpain 3 (C3) announced today collaborative funding of a $300,000 research grant to...
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Coave Therapeutics Receives Grant from the ALS Association to Advance its CTx-TFEB Program as a Potential Treatment for All Forms of ALS
February 29, 2024 07:00 ET | Coave Therapeutics
CTx-TFEB is a novel, targeted genetic medicine approach designed to promote autophagy and reduce the accumulation of toxic protein aggregates in neurons Funding aims to support the progression of...
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Wave Life Sciences Announces Initiation of Dosing in RestorAATion Clinical Program Evaluating First-Ever RNA Editing Candidate, WVE-006, for Alpha-1 Antitrypsin Deficiency
December 06, 2023 16:08 ET | Wave Life Sciences USA, Inc.
Wave Life Sciences Announces Initiation of Dosing in Clinical Trial Evaluating First-Ever RNA Editing Candidate, WVE-006, in Alpha-1 Antitrypsin Deficiency
FDA approves muscula
FDA approves muscular dystrophy drug built on Children’s National research
October 27, 2023 09:27 ET | Children's National Hospital
WASHINGTON, D.C., Oct. 27, 2023 (GLOBE NEWSWIRE) -- Boys with Duchenne muscular dystrophy (DMD) have a clinically proven, new treatment option with the Food and Drug Administration’s approval...
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Coave Therapeutics to Present at Upcoming Conferences
September 28, 2023 08:15 ET | Coave Therapeutics
Paris, France, September 28, 2023 – Coave Therapeutics (‘Coave’), a genetic medicine company focused on developing life-changing therapies for CNS (Central Nervous System) and eye diseases, announces...
FDA Drug Approval for Duchenne Muscular Dystrophy
Muscular Dystrophy Association Celebrates FDA Approval of Sarepta Therapeutics’ ELEVIDYS for Treatment of Duchenne Muscular Dystrophy
June 22, 2023 15:31 ET | Muscular Dystrophy Association
New York, June 22, 2023 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) celebrates the US Food and Drug Administration (FDA) accelerated approval of ELEVIDYS (delandistrogene...
MDA Announces Gene Therapy Support Network
Muscular Dystrophy Association Announces Gene Therapy Support Network for Families Living with Neuromuscular Disease
May 22, 2023 14:48 ET | Muscular Dystrophy Association
New York, May 22, 2023 (GLOBE NEWSWIRE) -- Muscular Dystrophy Association (MDA) announced today the launch of the MDA Gene Therapy Support Network (GTx), ahead of a pending FDA approval for the...
MDA Research Grants for Duchenne Muscular Dystrophy
Muscular Dystrophy Association Announces Nearly $400K in Research Grants to Address Challenges in Duchenne Muscular Dystrophy Gene Therapy
March 13, 2023 09:00 ET | Muscular Dystrophy Association
New York, NY, March 13, 2023 (GLOBE NEWSWIRE) -- Today, Muscular Dystrophy Association (MDA) announced two research grants designed to address potential transgene-triggered safety concerns in...